Ultragenyx Pharmaceutical Inc. is a biopharmaceutical company. The Company is focused on the identification, acquisition, development, and commercialization of novel products for the treatment of serious rare and ultrarare genetic diseases. Its therapies and clinical-stage pipeline consist of four product categories: biologics, small molecules, AAV gene therapy, and nucleic acid product candidates. Its four approved product candidates include Crysvita (burosumab) for the treatment of X-linked hypophosphatemia (XLH), and tumor-induced osteomalacia (TIO), Mepsevii (vestronidase alfa) for the treatment of mucopolysaccharidosis VII (MPSVII) or Sly Syndrome, Dojolvi (triheptanoin) for the treatment of long-chain fatty acid oxidation disorders (LC-FAOD), and Evkeeza (evinacumab) for the treatment of homozygous familial hypercholesterolemia (HoFH). Its clinical product candidates include DTX401, DTX301, UX701, UX143, UX111, and GTX-102. UX143 for the treatment of Osteogenesis Imperfecta.
企業コードRARE
会社名Ultragenyx Pharmaceutical Inc
上場日Jan 31, 2014
設立日2011
最高経営責任者「CEO」Dr. Emil D. Kakkis, M.D., Ph.D.
従業員数1294
証券種類Ordinary Share
決算期末Jan 31
本社所在地60 Leveroni Ct
都市NOVATO
証券取引所NASDAQ Global Select Consolidated
国United States of America
郵便番号94949
電話番号14154838800
ウェブサイトhttps://www.ultragenyx.com/
企業コードRARE
上場日Jan 31, 2014
設立日2011
過去5年間の配当金総支払額は
0.00
米ドルである。

データなし