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Ultragenyx Pharmaceutical Inc

RARE

29.560USD

+0.290+0.99%
收盤 08/26, 16:00美東報價延遲15分鐘
2.85B總市值
虧損本益比TTM

Ultragenyx Pharmaceutical Inc

29.560

+0.290+0.99%
關於 Ultragenyx Pharmaceutical Inc 公司
Ultragenyx Pharmaceutical Inc. 是一家生物製藥公司。該公司專注於識別、收購、開發和商業化用於治療嚴重罕見和極罕見遺傳病的新產品。其療法和臨牀階段產品線包括四類產品:生物製劑、小分子、AAV 基因治療和核酸候選產品。該公司的四種獲批候選產品包括用於治療 X 連鎖低磷血癥 (XLH) 和腫瘤誘發性骨軟化症 (TIO) 的 Crysvita (burosumab)、用於治療粘多糖貯積症 VII (MPSVII) 或 Sly 綜合徵的 Mepsevii (vestronidase alfa)、用於治療長鏈脂肪酸氧化障礙 (LC-FAOD) 的 Dojorvi (triheptanoin) 和用於治療純閤家族性高膽固醇血癥 (HoFH) 的 Evkeeza (evinacumab)。其臨牀候選產品包括DTX401、DTX301和UX701。DTX401用於治療Ia型糖原累積病。
公司簡介
公司代碼RARE
公司名稱Ultragenyx Pharmaceutical Inc
上市日期Jan 31, 2014
CEODr. Emil D. Kakkis, M.D., Ph.D.
員工數量1294
證券類型Ordinary Share
年結日Jan 31
公司地址60 Leveroni Ct
城市NOVATO
上市交易所NASDAQ Global Select Consolidated
國家United States of America
郵編94949
電話14154838800
網址https://www.ultragenyx.com/
公司代碼RARE
上市日期Jan 31, 2014
CEODr. Emil D. Kakkis, M.D., Ph.D.
公司高階主管
名稱
名稱/職務
職務
持股
持股變動
Dr. Emil D. Kakkis, M.D., Ph.D.
Dr. Emil D. Kakkis, M.D., Ph.D.
President, Chief Executive Officer, Director
President, Chief Executive Officer, Director
2.69M
-1.17%
Mr. Dennis Karl Huang
Mr. Dennis Karl Huang
Executive Vice President, Chief Technical Operations Officer, Gene Therapy Operations
Executive Vice President, Chief Technical Operations Officer, Gene Therapy Operations
107.20K
+41.78%
Mr. Erik Harris
Mr. Erik Harris
Executive Vice President, Chief Commercial Officer
Executive Vice President, Chief Commercial Officer
41.99K
+83.47%
Mr. Daniel G. Welch
Mr. Daniel G. Welch
Independent Chairman of the Board
Independent Chairman of the Board
27.34K
+26.57%
Mr. Michael A. Narachi
Mr. Michael A. Narachi
Independent Director
Independent Director
27.34K
+26.57%
Dr. Shehnaaz Suliman, M.D.
Dr. Shehnaaz Suliman, M.D.
Independent Director
Independent Director
20.59K
+38.64%
Dr. Amrit Ray, M.D.
Dr. Amrit Ray, M.D.
Independent Director
Independent Director
18.02K
+46.74%
Mr. Howard Horn
Mr. Howard Horn
Chief Financial Officer, Executive Vice President, Corporate Strategy
Chief Financial Officer, Executive Vice President, Corporate Strategy
15.69K
-83.00%
Mr. John R. Pinion, II
Mr. John R. Pinion, II
Chief Quality Officer, Executive Vice President - Translational Sciences
Chief Quality Officer, Executive Vice President - Translational Sciences
--
--
Dr. Deborah L. Dunsire, M.D.
Dr. Deborah L. Dunsire, M.D.
Independent Director
Independent Director
--
--
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名稱
名稱/職務
職務
持股
持股變動
Dr. Emil D. Kakkis, M.D., Ph.D.
Dr. Emil D. Kakkis, M.D., Ph.D.
President, Chief Executive Officer, Director
President, Chief Executive Officer, Director
2.69M
-1.17%
Mr. Dennis Karl Huang
Mr. Dennis Karl Huang
Executive Vice President, Chief Technical Operations Officer, Gene Therapy Operations
Executive Vice President, Chief Technical Operations Officer, Gene Therapy Operations
107.20K
+41.78%
Mr. Erik Harris
Mr. Erik Harris
Executive Vice President, Chief Commercial Officer
Executive Vice President, Chief Commercial Officer
41.99K
+83.47%
Mr. Daniel G. Welch
Mr. Daniel G. Welch
Independent Chairman of the Board
Independent Chairman of the Board
27.34K
+26.57%
Mr. Michael A. Narachi
Mr. Michael A. Narachi
Independent Director
Independent Director
27.34K
+26.57%
Dr. Shehnaaz Suliman, M.D.
Dr. Shehnaaz Suliman, M.D.
Independent Director
Independent Director
20.59K
+38.64%
收入明細
單位: USD更新時間: 7月6日 週日
單位: USD更新時間: 7月6日 週日
FY2025Q1
FY2024
FY2024Q4
FY2024Q3
FY2024Q2
FY2024Q1
FY2023
FY2023Q4
FY2023Q3
FY2023Q2
FY2023Q1
FY2022
FY2022Q4
FY2022Q3
FY2022Q2
FY2021
FY2020
業務USD
名稱
營收
佔比
Crysvita
55.08M
39.54%
Crysvita royalty revenue
47.78M
34.31%
Dojolvi
17.01M
12.21%
Evkeeza
11.03M
7.92%
Mepsevii
8.39M
6.02%
地區USD
名稱
營收
佔比
North America
57.79M
41.49%
Latin America
54.89M
39.40%
Europe
23.33M
16.75%
Japan
3.29M
2.36%
業務
地區
業務USD
名稱
營收
佔比
Crysvita
55.08M
39.54%
Crysvita royalty revenue
47.78M
34.31%
Dojolvi
17.01M
12.21%
Evkeeza
11.03M
7.92%
Mepsevii
8.39M
6.02%
股東統計
更新時間: 8月15日 週五
更新時間: 8月15日 週五
持股股東
股東類型
持股股東
持股股東
佔比
The Vanguard Group, Inc.
10.58%
BlackRock Institutional Trust Company, N.A.
5.21%
Sands Capital Management, LLC
4.09%
T. Rowe Price Associates, Inc.
2.91%
Baker Bros. Advisors LP
2.88%
其他
74.34%
持股股東
持股股東
佔比
The Vanguard Group, Inc.
10.58%
BlackRock Institutional Trust Company, N.A.
5.21%
Sands Capital Management, LLC
4.09%
T. Rowe Price Associates, Inc.
2.91%
Baker Bros. Advisors LP
2.88%
其他
74.34%
股東類型
持股股東
佔比
Investment Advisor
44.50%
Investment Advisor/Hedge Fund
31.79%
Hedge Fund
20.00%
Individual Investor
3.50%
Research Firm
1.33%
Private Equity
1.31%
Sovereign Wealth Fund
1.02%
Bank and Trust
0.67%
Pension Fund
0.63%
機構持股
更新時間: 7月1日 週二
更新時間: 7月1日 週二
報告期間
機構數
持股數
持股佔比
持股變動
2025Q2
635
97.48M
101.32%
-2.63M
2025Q1
652
96.83M
102.45%
-3.19M
2024Q4
645
94.29M
102.32%
-4.54M
2024Q3
633
93.51M
101.49%
-6.93M
2024Q2
618
95.17M
101.90%
+3.05M
2024Q1
605
86.17M
101.67%
-4.74M
2023Q4
588
86.44M
105.27%
+5.64M
2023Q3
574
75.90M
106.07%
-3.60M
2023Q2
591
75.05M
105.07%
-3.13M
2023Q1
609
74.12M
105.56%
-2.85M
查看更多
股東持股明細
名稱
持股數
佔比
持股變動
變動比例
公告日期
The Vanguard Group, Inc.
9.98M
10.55%
-38.64K
-0.39%
Mar 31, 2025
BlackRock Institutional Trust Company, N.A.
4.91M
5.2%
-49.62K
-1.00%
Mar 31, 2025
Sands Capital Management, LLC
4.16M
4.4%
-134.44K
-3.13%
Mar 31, 2025
T. Rowe Price Associates, Inc.
3.14M
3.32%
+698.80K
+28.65%
Mar 31, 2025
Baker Bros. Advisors LP
1.58M
1.67%
--
--
Mar 31, 2025
Kakkis (Emil D)
2.69M
2.85%
-31.78K
-1.17%
Mar 07, 2025
State Street Global Advisors (US)
2.62M
2.77%
-104.13K
-3.82%
Mar 31, 2025
Suvretta Capital Management, LLC
2.02M
2.14%
+873.19K
+75.84%
Mar 31, 2025
查看更多
持股ETF
更新時間: 8月6日 週三
更新時間: 8月6日 週三
機構名稱
佔比
Global X Genomics & Biotechnology ETF
2.76%
Motley Fool Small-Cap Growth ETF
2.3%
Franklin Genomic Advancements ETF
1.5%
Motley Fool Mid-Cap Growth ETF
1.49%
Virtus LifeSci Biotech Products ETF
1.34%
WisdomTree BioRevolution Fund
1.18%
Touchstone Sands Capital US Select Growth ETF
0.96%
Goldman Sachs Future Health Care Equity ETF
0.64%
Putnam Sustainable Future ETF
0.58%
SPDR S&P Biotech ETF
0.56%
查看更多
Global X Genomics & Biotechnology ETF
佔比2.76%
Motley Fool Small-Cap Growth ETF
佔比2.3%
Franklin Genomic Advancements ETF
佔比1.5%
Motley Fool Mid-Cap Growth ETF
佔比1.49%
Virtus LifeSci Biotech Products ETF
佔比1.34%
WisdomTree BioRevolution Fund
佔比1.18%
Touchstone Sands Capital US Select Growth ETF
佔比0.96%
Goldman Sachs Future Health Care Equity ETF
佔比0.64%
Putnam Sustainable Future ETF
佔比0.58%
SPDR S&P Biotech ETF
佔比0.56%
分紅派息
近5年累計派現 0.00 美元
公告日期
分紅計劃
股權登記日
現金發放日
除權除息日
暫無數據
拆合股
公告日期
類型
比率
暫無數據
公告日期
類型
比率
暫無數據
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