REGENXBIO Inc. is a clinical-stage biotechnology company seeking to improve lives through the curative potential of gene therapy. The Company has developed a pipeline of gene therapy programs using its proprietary adeno-associated virus (AAV) gene therapy delivery platform (NAV Technology Platform) to address genetic diseases. It is focused on its internal development pipeline in three areas: retinal, neuromuscular, and neurodegenerative diseases. Its investigational AAV therapeutics include ABBV-RGX-314, RGX-202, RGX-121, and RGX-111. It is developing ABBV-RGX-314 in collaboration with AbbVie to treat large patient populations impacted by wet age-related macular degeneration, diabetic retinopathy (DR) and other chronic retinal diseases characterized by loss of vision. It is developing RGX-202 to treat Duchenne muscular dystrophy (Duchenne). The Company is developing RGX-121 to treat Mucopolysaccharidosis type II (MPS II), a progressive, neurodegenerative lysosomal storage disorder.
公司代码RGNX
公司名称Regenxbio Inc
上市日期Sep 17, 2015
CEOSimpson (Curran M)
员工数量353
证券类型Ordinary Share
年结日Sep 17
公司地址9804 Medical Center Drive
城市ROCKVILLE
上市交易所NASDAQ OMX - NASDAQ BASIC
国家United States of America
邮编20850
电话12405528181
网址https://regenxbio.com/
公司代码RGNX
上市日期Sep 17, 2015
CEOSimpson (Curran M)