REGENXBIO Inc. is a clinical-stage biotechnology company seeking to improve lives through the curative potential of gene therapy. The Company has developed a pipeline of gene therapy programs using its proprietary adeno-associated virus (AAV) gene therapy delivery platform (NAV Technology Platform) to address genetic diseases. The Company is focused on its internal development pipeline in three areas: retinal, neuromuscular and neurodegenerative diseases. Its investigational AAV therapeutics include ABBV-RGX-314, RGX-202 and RGX-121. It is developing ABBV-RGX-314 in collaboration with AbbVie to treat large patient populations impacted by wet age-related macular degeneration, diabetic retinopathy (DR) and other chronic retinal diseases characterized by loss of vision. It is developing RGX-202 to treat Duchenne muscular dystrophy (Duchenne). The Company is developing RGX-121 to treat Mucopolysaccharidosis type II (MPS II), a progressive, neurodegenerative lysosomal storage disorder.
Em Crescimento
A empresa está em fase de crescimento, com a receita anual mais recente totalizando US$ 83.33M.
Subavaliada
O PE mais recente da empresa é -3.24, em uma faixa percentil baixa de 3 anos.
Venda Institucional
As participações institucionais mais recentes são de 44.17M ações, uma redução de 11.92% em relação ao trimestre anterior.
Mantido por PRFDX
O Super Investidor PRFDX possui 18.51K ações desta empresa.