Ultragenyx Pharmaceutical Inc. is a biopharmaceutical company. The Company is focused on the identification, acquisition, development, and commercialization of novel products for the treatment of serious rare and ultrarare genetic diseases. Its therapies and clinical-stage pipeline consist of four product categories: biologics, small molecules, AAV gene therapy, and nucleic acid product candidates. Its four approved product candidates include Crysvita (burosumab) for the treatment of X-linked hypophosphatemia (XLH), and tumor-induced osteomalacia (TIO), Mepsevii (vestronidase alfa) for the treatment of mucopolysaccharidosis VII (MPSVII) or Sly Syndrome, Dojolvi (triheptanoin) for the treatment of long-chain fatty acid oxidation disorders (LC-FAOD), and Evkeeza (evinacumab) for the treatment of homozygous familial hypercholesterolemia (HoFH). Its clinical product candidates include DTX401, DTX301, UX701, UX143, UX111, and GTX-102. UX143 for the treatment of Osteogenesis Imperfecta.
Código da empresaRARE
Nome da EmpresaUltragenyx Pharmaceutical Inc
Data de listagemJan 31, 2014
Fundado em2011
CEODr. Emil D. Kakkis, M.D., Ph.D.
Número de funcionários1294
Tipo de títulosOrdinary Share
Fim do ano fiscalJan 31
Endereço60 Leveroni Ct
CidadeNOVATO
Bolsa de valoresNASDAQ Global Select Consolidated
PaísUnited States of America
Código postal94949
Telefone14154838800
Sitehttps://www.ultragenyx.com/
Código da empresaRARE
Data de listagemJan 31, 2014
Fundado em2011
Um total de
0.00
USD foi distribuído em dividendos nos últimos 5 anos.

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