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Ultragenyx Pharmaceutical Inc

RARE
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26.265USD
-0.195-0.74%
Horarios del mercado ETCotizaciones retrasadas 15 min
2.58BCap. mercado
PérdidaP/E TTM

Ultragenyx Pharmaceutical Inc

26.265
-0.195-0.74%

Más Datos de Ultragenyx Pharmaceutical Inc Compañía

Ultragenyx Pharmaceutical Inc. is a biopharmaceutical company. The Company is focused on the identification, acquisition, development, and commercialization of novel products for the treatment of serious rare and ultrarare genetic diseases. Its therapies and clinical-stage pipeline consist of four product categories: biologics, small molecules, AAV gene therapy, and nucleic acid product candidates. Its four approved product candidates include Crysvita (burosumab) for the treatment of X-linked hypophosphatemia (XLH), and tumor-induced osteomalacia (TIO), Mepsevii (vestronidase alfa) for the treatment of mucopolysaccharidosis VII (MPSVII) or Sly Syndrome, Dojolvi (triheptanoin) for the treatment of long-chain fatty acid oxidation disorders (LC-FAOD), and Evkeeza (evinacumab) for the treatment of homozygous familial hypercholesterolemia (HoFH). Its clinical product candidates include DTX401, DTX301, UX701, UX143, UX111, and GTX-102. UX143 for the treatment of Osteogenesis Imperfecta.

Información de Ultragenyx Pharmaceutical Inc

Símbolo de cotizaciónRARE
Nombre de la empresaUltragenyx Pharmaceutical Inc
Fecha de salida a bolsaJan 31, 2014
Director ejecutivoKakkis (Emil D)
Número de empleados1294
Tipo de seguridadOrdinary Share
Fin del año fiscalJan 31
Dirección60 Leveroni Ct
CiudadNOVATO
Bolsa de valoresNASDAQ OMX - NASDAQ BASIC
PaísUnited States of America
Código postal94949
Teléfono14154838800
Sitio Webhttps://www.ultragenyx.com/
Símbolo de cotizaciónRARE
Fecha de salida a bolsaJan 31, 2014
Director ejecutivoKakkis (Emil D)

Ejecutivos de Ultragenyx Pharmaceutical Inc

Nombre
Nombre/Posición
Posición
Accionistas
Cambio
Dr. Emil D. Kakkis, M.D., Ph.D.
Dr. Emil D. Kakkis, M.D., Ph.D.
President, Chief Executive Officer, Director
President, Chief Executive Officer, Director
2.83M
+2.71%
Mr. Dennis Karl Huang
Mr. Dennis Karl Huang
Executive Vice President, Chief Technical Operations Officer, Gene Therapy Operations
Executive Vice President, Chief Technical Operations Officer, Gene Therapy Operations
140.45K
+16.46%
Mr. Erik Harris
Mr. Erik Harris
Executive Vice President, Chief Commercial Officer
Executive Vice President, Chief Commercial Officer
90.60K
+31.89%
Mr. Howard Horn
Mr. Howard Horn
Chief Financial Officer, Executive Vice President, Corporate Strategy
Chief Financial Officer, Executive Vice President, Corporate Strategy
48.72K
-9.61%
Mr. Michael A. Narachi
Mr. Michael A. Narachi
Independent Director
Independent Director
26.95K
-1.47%
Mr. Daniel G. Welch
Mr. Daniel G. Welch
Independent Chairman of the Board
Independent Chairman of the Board
26.95K
-1.47%
Dr. Shehnaaz Suliman, M.D.
Dr. Shehnaaz Suliman, M.D.
Independent Director
Independent Director
20.20K
-1.96%
Dr. Amrit Ray, M.D.
Dr. Amrit Ray, M.D.
Independent Director
Independent Director
17.63K
-2.24%
Mr. Matthew K. (Matt) Fust
Mr. Matthew K. (Matt) Fust
Independent Director
Independent Director
--
--
Mr. John R. Pinion, II
Mr. John R. Pinion, II
Chief Quality Officer, Executive Vice President - Translational Sciences
Chief Quality Officer, Executive Vice President - Translational Sciences
--
--
Ver más
Nombre
Nombre/Posición
Posición
Accionistas
Cambio
Dr. Emil D. Kakkis, M.D., Ph.D.
Dr. Emil D. Kakkis, M.D., Ph.D.
President, Chief Executive Officer, Director
President, Chief Executive Officer, Director
2.83M
+2.71%
Mr. Dennis Karl Huang
Mr. Dennis Karl Huang
Executive Vice President, Chief Technical Operations Officer, Gene Therapy Operations
Executive Vice President, Chief Technical Operations Officer, Gene Therapy Operations
140.45K
+16.46%
Mr. Erik Harris
Mr. Erik Harris
Executive Vice President, Chief Commercial Officer
Executive Vice President, Chief Commercial Officer
90.60K
+31.89%
Mr. Howard Horn
Mr. Howard Horn
Chief Financial Officer, Executive Vice President, Corporate Strategy
Chief Financial Officer, Executive Vice President, Corporate Strategy
48.72K
-9.61%
Mr. Michael A. Narachi
Mr. Michael A. Narachi
Independent Director
Independent Director
26.95K
-1.47%
Mr. Daniel G. Welch
Mr. Daniel G. Welch
Independent Chairman of the Board
Independent Chairman of the Board
26.95K
-1.47%

Desglose de ingresos

Divisa: USDActualizado: lun., 6 de abr
Divisa: USDActualizado: lun., 6 de abr
FY2025
FY2025Q4
FY2025Q3
FY2025Q2
FY2025Q1
FY2024
FY2024Q4
FY2024Q3
FY2024Q2
FY2024Q1
FY2023
FY2023Q4
FY2023Q3
FY2023Q2
FY2023Q1
FY2022
FY2022Q4
FY2022Q3
FY2022Q2
FY2021
FY2020
Por negocioUSD
Nombre
Ganancia
Proporción
Crysvita royalty revenue
304.00M
45.17%
Crysvita
177.00M
26.30%
Dojolvi
96.00M
14.26%
Evkeeza
59.00M
8.77%
Mepsevii
37.00M
5.50%
Por regiónUSD
Nombre
Ganancia
Proporción
North America
377.00M
56.02%
Latin America
170.00M
25.26%
Europe Middle East and Africa
108.00M
16.05%
Asia Pacific
18.00M
2.67%
Por negocio
Por región
Por negocioUSD
Nombre
Ganancia
Proporción
Crysvita royalty revenue
304.00M
45.17%
Crysvita
177.00M
26.30%
Dojolvi
96.00M
14.26%
Evkeeza
59.00M
8.77%
Mepsevii
37.00M
5.50%

Estadísticas de accionistas

Actualizado: dom., 10 de may
Actualizado: dom., 10 de may
Accionistas
Tipos de accionistas
Accionistas
Accionistas
Proporción
Vanguard Portfolio Management, LLC
5.47%
BlackRock Institutional Trust Company, N.A.
5.47%
State Street Investment Management (US)
5.10%
Vanguard Capital Management, LLC
4.25%
Sands Capital Management, LLC
3.26%
Otro
76.45%
Accionistas
Accionistas
Proporción
Vanguard Portfolio Management, LLC
5.47%
BlackRock Institutional Trust Company, N.A.
5.47%
State Street Investment Management (US)
5.10%
Vanguard Capital Management, LLC
4.25%
Sands Capital Management, LLC
3.26%
Otro
76.45%
Tipos de accionistas
Accionistas
Proporción
Investment Advisor
47.10%
Investment Advisor/Hedge Fund
25.80%
Hedge Fund
17.03%
Research Firm
4.75%
Individual Investor
3.79%
Sovereign Wealth Fund
1.28%
Venture Capital
0.51%
Pension Fund
0.44%
Bank and Trust
0.40%

Participación institucional

Actualizado: mié., 1 de abr
Actualizado: mié., 1 de abr
Periodo del informe
Número de instituciones
Acciones mantenidas
Proporción
Cambio
2026Q1
695
106.19M
107.82%
-1.32M
2025Q4
665
100.29M
103.96%
-2.21M
2025Q3
640
97.34M
100.90%
-3.53M
2025Q2
635
97.48M
101.32%
-2.63M
2025Q1
652
96.83M
102.45%
-3.19M
2024Q4
645
94.29M
102.32%
-4.54M
2024Q3
633
93.51M
101.49%
-6.93M
2024Q2
618
95.17M
101.90%
+3.05M
2024Q1
605
86.17M
101.67%
-4.74M
2023Q4
588
86.44M
105.27%
+5.64M
Ver más

Actividad de los accionistas

Nombre
Acciones mantenidas
Proporción
Cambio
Cambio %
Fecha
BlackRock Institutional Trust Company, N.A.
5.07M
5.26%
+54.55K
+1.09%
Sep 30, 2025
State Street Investment Management (US)
3.69M
3.83%
+1.12M
+43.55%
Sep 30, 2025
Sands Capital Management, LLC
3.77M
3.91%
-173.63K
-4.40%
Sep 30, 2025
JP Morgan Asset Management
3.25M
3.37%
+644.31K
+24.74%
Sep 30, 2025
RTW Investments L.P.
3.26M
3.38%
+1.55M
+90.83%
Sep 30, 2025
Kakkis (Emil D)
2.69M
2.79%
-31.78K
-1.17%
Mar 07, 2025
Baker Bros. Advisors LP
2.77M
2.87%
--
--
Sep 30, 2025
Wellington Management Company, LLP
1.95M
2.02%
+73.31K
+3.92%
Sep 30, 2025
Ver más

ETFs relacionados

Actualizado: mar., 2 de dic
Actualizado: mar., 2 de dic
Nombre
Proporción
Motley Fool Small-Cap Growth ETF
3.73%
Global X Genomics & Biotechnology ETF
3.19%
Franklin Genomic Advancements ETF
1.59%
Virtus LifeSci Biotech Products ETF
1.41%
State Street SPDR S&P Biotech ETF
1.32%
WisdomTree BioRevolution Fund
0.94%
Direxion Daily S&P Biotech Bull 3X Shares
0.81%
Touchstone Sands Capital US Select Growth ETF
0.8%
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0.6%
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0.54%
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Motley Fool Small-Cap Growth ETF
Proporción3.73%
Global X Genomics & Biotechnology ETF
Proporción3.19%
Franklin Genomic Advancements ETF
Proporción1.59%
Virtus LifeSci Biotech Products ETF
Proporción1.41%
State Street SPDR S&P Biotech ETF
Proporción1.32%
WisdomTree BioRevolution Fund
Proporción0.94%
Direxion Daily S&P Biotech Bull 3X Shares
Proporción0.81%
Touchstone Sands Capital US Select Growth ETF
Proporción0.8%
Goldman Sachs Future Health Care Equity ETF
Proporción0.6%
First Trust Multi-Manager Large Growth ETF
Proporción0.54%

Dividendos

Un total de 0.00 USD se ha distribuido en dividendos durante los últimos 5 años.
Fecha
Dividendos
Fecha de registro
Fecha de pago
Fecha ex-dividendo
Sin datos

División de acciones

Fecha
Fecha ex-dividendo
Tipo
Relación
Sin datos
Fecha
Fecha ex-dividendo
Tipo
Relación
Sin datos
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