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Ultragenyx Pharmaceutical Inc

RARE
24.700USD
+0.910+3.83%
Cierre 02/06, 16:00ETCotizaciones retrasadas 15 min
2.38BCap. mercado
PérdidaP/E TTM

Ultragenyx Pharmaceutical Inc

24.700
+0.910+3.83%

Más Datos de Ultragenyx Pharmaceutical Inc Compañía

Ultragenyx Pharmaceutical Inc. is a biopharmaceutical company. The Company is focused on the identification, acquisition, development, and commercialization of novel products for the treatment of serious rare and ultrarare genetic diseases. Its therapies and clinical-stage pipeline consist of four product categories: biologics, small molecules, AAV gene therapy, and nucleic acid product candidates. Its four approved product candidates include Crysvita (burosumab) for the treatment of X-linked hypophosphatemia (XLH), and tumor-induced osteomalacia (TIO), Mepsevii (vestronidase alfa) for the treatment of mucopolysaccharidosis VII (MPSVII) or Sly Syndrome, Dojolvi (triheptanoin) for the treatment of long-chain fatty acid oxidation disorders (LC-FAOD), and Evkeeza (evinacumab) for the treatment of homozygous familial hypercholesterolemia (HoFH). Its clinical product candidates include DTX401, DTX301, UX701, UX143, UX111, and GTX-102. UX143 for the treatment of Osteogenesis Imperfecta.

Información de Ultragenyx Pharmaceutical Inc

Símbolo de cotizaciónRARE
Nombre de la empresaUltragenyx Pharmaceutical Inc
Fecha de salida a bolsaJan 31, 2014
Director ejecutivoKakkis (Emil D)
Número de empleados1294
Tipo de seguridadOrdinary Share
Fin del año fiscalJan 31
Dirección60 Leveroni Ct
CiudadNOVATO
Bolsa de valoresNASDAQ OMX - NASDAQ BASIC
PaísUnited States of America
Código postal94949
Teléfono14154838800
Sitio Webhttps://www.ultragenyx.com/
Símbolo de cotizaciónRARE
Fecha de salida a bolsaJan 31, 2014
Director ejecutivoKakkis (Emil D)

Ejecutivos de Ultragenyx Pharmaceutical Inc

Nombre
Nombre/Posición
Posición
Accionistas
Cambio
Dr. Emil D. Kakkis, M.D., Ph.D.
Dr. Emil D. Kakkis, M.D., Ph.D.
President, Chief Executive Officer, Director
President, Chief Executive Officer, Director
2.69M
-31783.00%
Mr. Dennis Karl Huang
Mr. Dennis Karl Huang
Executive Vice President, Chief Technical Operations Officer, Gene Therapy Operations
Executive Vice President, Chief Technical Operations Officer, Gene Therapy Operations
107.20K
+31589.00%
Mr. Erik Harris
Mr. Erik Harris
Executive Vice President, Chief Commercial Officer
Executive Vice President, Chief Commercial Officer
41.99K
+19104.00%
Mr. Michael A. Narachi
Mr. Michael A. Narachi
Independent Director
Independent Director
27.34K
+5740.00%
Mr. Daniel G. Welch
Mr. Daniel G. Welch
Independent Chairman of the Board
Independent Chairman of the Board
27.34K
+5740.00%
Dr. Shehnaaz Suliman, M.D.
Dr. Shehnaaz Suliman, M.D.
Independent Director
Independent Director
20.59K
+5740.00%
Dr. Amrit Ray, M.D.
Dr. Amrit Ray, M.D.
Independent Director
Independent Director
18.02K
+5740.00%
Mr. Howard Horn
Mr. Howard Horn
Chief Financial Officer, Executive Vice President, Corporate Strategy
Chief Financial Officer, Executive Vice President, Corporate Strategy
1.52K
-3150.00%
Mr. Matthew K. (Matt) Fust
Mr. Matthew K. (Matt) Fust
Independent Director
Independent Director
--
--
Mr. John R. Pinion, II
Mr. John R. Pinion, II
Chief Quality Officer, Executive Vice President - Translational Sciences
Chief Quality Officer, Executive Vice President - Translational Sciences
--
--
Ver más
Nombre
Nombre/Posición
Posición
Accionistas
Cambio
Dr. Emil D. Kakkis, M.D., Ph.D.
Dr. Emil D. Kakkis, M.D., Ph.D.
President, Chief Executive Officer, Director
President, Chief Executive Officer, Director
2.69M
-31783.00%
Mr. Dennis Karl Huang
Mr. Dennis Karl Huang
Executive Vice President, Chief Technical Operations Officer, Gene Therapy Operations
Executive Vice President, Chief Technical Operations Officer, Gene Therapy Operations
107.20K
+31589.00%
Mr. Erik Harris
Mr. Erik Harris
Executive Vice President, Chief Commercial Officer
Executive Vice President, Chief Commercial Officer
41.99K
+19104.00%
Mr. Michael A. Narachi
Mr. Michael A. Narachi
Independent Director
Independent Director
27.34K
+5740.00%
Mr. Daniel G. Welch
Mr. Daniel G. Welch
Independent Chairman of the Board
Independent Chairman of the Board
27.34K
+5740.00%
Dr. Shehnaaz Suliman, M.D.
Dr. Shehnaaz Suliman, M.D.
Independent Director
Independent Director
20.59K
+5740.00%

Desglose de ingresos

Divisa: USDActualizado: mar., 6 de ene
Divisa: USDActualizado: mar., 6 de ene
FY2025Q3
FY2025Q2
FY2025Q1
FY2024
FY2024Q4
FY2024Q3
FY2024Q2
FY2024Q1
FY2023
FY2023Q4
FY2023Q3
FY2023Q2
FY2023Q1
FY2022
FY2022Q4
FY2022Q3
FY2022Q2
FY2021
FY2020
Por negocioUSD
Nombre
Ganancia
Proporción
Crysvita royalty revenue
64.94M
40.60%
Crysvita
47.00M
29.39%
Dojolvi
24.27M
15.18%
Evkeeza
16.72M
10.45%
Mepsevii
7.00M
4.38%
Por regiónUSD
Nombre
Ganancia
Proporción
North America
83.54M
52.23%
Latin America
43.36M
27.11%
Europe
27.88M
17.43%
Asia Pacific
5.15M
3.22%
Por negocio
Por región
Por negocioUSD
Nombre
Ganancia
Proporción
Crysvita royalty revenue
64.94M
40.60%
Crysvita
47.00M
29.39%
Dojolvi
24.27M
15.18%
Evkeeza
16.72M
10.45%
Mepsevii
7.00M
4.38%

Estadísticas de accionistas

Actualizado: sáb., 7 de feb
Actualizado: sáb., 7 de feb
Accionistas
Tipos de accionistas
Accionistas
Accionistas
Proporción
The Vanguard Group, Inc.
10.62%
BlackRock Institutional Trust Company, N.A.
5.26%
Fidelity Management & Research Company LLC
4.07%
Sands Capital Management, LLC
3.91%
State Street Investment Management (US)
3.83%
Otro
72.32%
Accionistas
Accionistas
Proporción
The Vanguard Group, Inc.
10.62%
BlackRock Institutional Trust Company, N.A.
5.26%
Fidelity Management & Research Company LLC
4.07%
Sands Capital Management, LLC
3.91%
State Street Investment Management (US)
3.83%
Otro
72.32%
Tipos de accionistas
Accionistas
Proporción
Investment Advisor
52.00%
Investment Advisor/Hedge Fund
31.58%
Hedge Fund
14.45%
Individual Investor
3.48%
Research Firm
2.31%
Sovereign Wealth Fund
1.02%
Private Equity
1.02%
Pension Fund
0.82%
Bank and Trust
0.43%

Participación institucional

Actualizado: jue., 1 de ene
Actualizado: jue., 1 de ene
Periodo del informe
Número de instituciones
Acciones mantenidas
Proporción
Cambio
2025Q4
665
100.29M
103.96%
-2.21M
2025Q3
640
97.34M
100.90%
-3.53M
2025Q2
635
97.48M
101.32%
-2.63M
2025Q1
652
96.83M
102.45%
-3.19M
2024Q4
645
94.29M
102.32%
-4.54M
2024Q3
633
93.51M
101.49%
-6.93M
2024Q2
618
95.17M
101.90%
+3.05M
2024Q1
605
86.17M
101.67%
-4.74M
2023Q4
588
86.44M
105.27%
+5.64M
2023Q3
574
75.90M
106.07%
-3.60M
Ver más

Actividad de los accionistas

Nombre
Acciones mantenidas
Proporción
Cambio
Cambio %
Fecha
The Vanguard Group, Inc.
10.11M
10.48%
-80.69K
-0.79%
Sep 30, 2025
BlackRock Institutional Trust Company, N.A.
5.07M
5.26%
+54.55K
+1.09%
Sep 30, 2025
Fidelity Management & Research Company LLC
3.92M
4.07%
+1.65M
+72.84%
Sep 30, 2025
Sands Capital Management, LLC
3.77M
3.91%
-173.63K
-4.40%
Sep 30, 2025
State Street Investment Management (US)
3.69M
3.83%
+1.12M
+43.55%
Sep 30, 2025
RTW Investments L.P.
3.26M
3.38%
+1.55M
+90.83%
Sep 30, 2025
JP Morgan Asset Management
3.25M
3.37%
+644.31K
+24.74%
Sep 30, 2025
Fidelity Institutional Asset Management
3.36M
3.48%
+3.02M
+906.25%
Sep 30, 2025
Baker Bros. Advisors LP
2.77M
2.87%
--
--
Sep 30, 2025
Kakkis (Emil D)
2.69M
2.79%
-31.78K
-1.17%
Mar 07, 2025
Ver más

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Actualizado: mar., 2 de dic
Actualizado: mar., 2 de dic
Nombre
Proporción
Motley Fool Small-Cap Growth ETF
3.73%
Global X Genomics & Biotechnology ETF
3.19%
Franklin Genomic Advancements ETF
1.59%
Virtus LifeSci Biotech Products ETF
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Motley Fool Small-Cap Growth ETF
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Global X Genomics & Biotechnology ETF
Proporción3.19%
Franklin Genomic Advancements ETF
Proporción1.59%
Virtus LifeSci Biotech Products ETF
Proporción1.41%
State Street SPDR S&P Biotech ETF
Proporción1.32%
WisdomTree BioRevolution Fund
Proporción0.94%
Direxion Daily S&P Biotech Bull 3X Shares
Proporción0.81%
Touchstone Sands Capital US Select Growth ETF
Proporción0.8%
Goldman Sachs Future Health Care Equity ETF
Proporción0.6%
First Trust Multi-Manager Large Growth ETF
Proporción0.54%

Dividendos

Un total de 0.00 USD se ha distribuido en dividendos durante los últimos 5 años.
Fecha
Dividendos
Fecha de registro
Fecha de pago
Fecha ex-dividendo
Sin datos

División de acciones

Fecha
Fecha ex-dividendo
Tipo
Relación
Sin datos
Fecha
Fecha ex-dividendo
Tipo
Relación
Sin datos
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