Ultragenyx Pharmaceutical Inc. is a biopharmaceutical company. The Company is focused on the identification, acquisition, development, and commercialization of novel products for the treatment of serious rare and ultrarare genetic diseases. Its therapies and clinical-stage pipeline consist of four product categories: biologics, small molecules, AAV gene therapy, and nucleic acid product candidates. Its four approved product candidates include Crysvita (burosumab) for the treatment of X-linked hypophosphatemia (XLH), and tumor-induced osteomalacia (TIO), Mepsevii (vestronidase alfa) for the treatment of mucopolysaccharidosis VII (MPSVII) or Sly Syndrome, Dojolvi (triheptanoin) for the treatment of long-chain fatty acid oxidation disorders (LC-FAOD), and Evkeeza (evinacumab) for the treatment of homozygous familial hypercholesterolemia (HoFH). Its clinical product candidates include DTX401, DTX301, UX701, UX143, UX111, and GTX-102. UX143 for the treatment of Osteogenesis Imperfecta.
BörsenkürzelRARE
Name des UnternehmensUltragenyx Pharmaceutical Inc
IPO-datumJan 31, 2014
Gegründet am2011
CEODr. Emil D. Kakkis, M.D., Ph.D.
Anzahl der mitarbeiter1294
WertpapierartOrdinary Share
GeschäftsjahresendeJan 31
Addresse60 Leveroni Ct
StadtNOVATO
BörseNASDAQ Global Select Consolidated
LandUnited States of America
Postleitzahl94949
Telefon14154838800
Websitehttps://www.ultragenyx.com/
BörsenkürzelRARE
IPO-datumJan 31, 2014
Gegründet am2011
In den vergangenen 5 Jahren wurden insgesamt
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