Ultragenyx Pharmaceutical Inc. is a biopharmaceutical company. The Company is focused on the identification, acquisition, development, and commercialization of novel products for the treatment of serious rare and ultrarare genetic diseases. Its therapies and clinical-stage pipeline consist of four product categories: biologics, small molecules, AAV gene therapy, and nucleic acid product candidates. Its four approved product candidates include Crysvita (burosumab) for the treatment of X-linked hypophosphatemia (XLH), and tumor-induced osteomalacia (TIO), Mepsevii (vestronidase alfa) for the treatment of mucopolysaccharidosis VII (MPSVII) or Sly Syndrome, Dojolvi (triheptanoin) for the treatment of long-chain fatty acid oxidation disorders (LC-FAOD), and Evkeeza (evinacumab) for the treatment of homozygous familial hypercholesterolemia (HoFH). Its clinical product candidates include DTX401, DTX301, UX701, UX143, UX111, and GTX-102. UX143 for the treatment of Osteogenesis Imperfecta.
High Growth
The company's revenue has grown steadily over the past 3 years, averaging 54.98% year-on-year.
Fairly Valued
The company’s latest PE is -5.47, at a medium 3-year percentile range.
Institutional Selling
The latest institutional holdings are 106.19M shares, decreasing 1.22% quarter-over-quarter.
Held by Frank Sands
Star Investor Frank Sands holds 2.88M shares of this stock.
Higher Market Activity
The company has more investor interest, with a 20-day turnover ratio of 0.82.